ACTIVE: TSHA-102 REVEAL paediatric gene-therapy study – Canada, UK and USA

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Status: Active, not recruitingStudy: REVEAL paediatric study of TSHA-102
Registry number: NCT06152237
Countries: Canada, United Kingdom and United States
Participants: Females aged 5–8 years

What is being studied?
This early paediatric study is evaluating the safety and possible effectiveness of a one-time intrathecal dose of TSHA-102, an investigational regulated MECP2 gene therapy.

The study is continuing to follow participants but is not currently recruiting according to ClinicalTrials.gov.

Official study record: https://clinicaltrials.gov/study/NCT06152237

Information checked 3 September 2026. Gene therapy remains experimental, with potential serious and unknown risks. Families should use the official registry for updates and discuss questions with their specialist team.